NEW STEP BY STEP MAP FOR MUSCULAR DYSTROPHY TREATMENT

just lately, the antibiotic gentamicin has actually been tested in boys with DMD, about 10% of whom have inherited a dystrophin gene using a untimely stop codon that halts the synthesis from the protein N-terminal on the dystroglycan binding region. Gentamicin suppresses chain termination, allowing for some complete-duration dystrophin to generally